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RNA InterferenceGene SilencingSmall Interfering RNASmall Interfering RNAsShort Hairpin RNAGene TherapyRNA-Induced Silencing ComplexLibrary PublishingPublishing MediaMammalian Cellsin VivoLentiviral VectorCatalytic Nucleic AcidssiRNA DeliveryCongenital Myasthenic SyndromeMyasthenic SyndromeEnhanced Green Fluorescent ProteinSignal Transducer and Activator of TranscriptionsiRNA TechnologyINHERITED DISORDERS
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